Re:First UK child to receive gene therapy for fatal genetic ...
by Traubenfuchs on Friday February 17, 2023 @04:51PM
(#34841078)
In this specific case CRISPR-CAS9 was used to edit "hematopoietic stem and progenitor cells". This means all modified stem cells (sadly not 100% of them) will from now on produce cells with the gene bugfix applied.
This does not imply that germ line cells were changed and COULD mean the person could still have a high risk of making children with the original gene defect.
This does not imply that germ line cells were changed and COULD mean the person could still have a high risk of making children with the original gene defect.
https://pubmed.ncbi.nlm.nih.gov/34882002/