Re:7/67 Children Receiving Skysona Gene Therapy Develop Bloo...
by mlyle on Thursday October 10, 2024 @01:35AM
(#41795859)
We didn't expect the rate of oncogenesis from off-target gene insertion. It's bad news.
At the same time, this is a treatment for a terrible, terrible disease; so far the consequences seem smaller than what cerebral adrenoleukodystrophy would deal out on its own.
So it's bad news about something which is probably still a good therapy (but we sure would like a better one).
At the same time, this is a treatment for a terrible, terrible disease; so far the consequences seem smaller than what cerebral adrenoleukodystrophy would deal out on its own.
So it's bad news about something which is probably still a good therapy (but we sure would like a better one).