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A comment on FDA approves first test of CRISPR for genetic defect causing sickle cell disease. Parent comment

Re:FDA approves first test of CRISPR for genetic defect caus... by maxerickson on Wednesday April 07, 2021 @10:51PM (#26734563)
This treatment modifies the adult hemoglobin gene.
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Re:FDA approves first test of CRISPR for genetic defect caus... by refurb on Thursday April 08, 2021 @10:28PM (#26746092)
That's what I get for not reading the article. But the point stands on correcting genetics for hematopoetic cells. It's possible to fix a small number of cells, then reimplant (often depleting the cells in the person first) and they will replicate.

Easier than trying to fix the cells in a solid organ.

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