395trek
Re:Couple pay >$800k for a gene-editing therapy for their daughter. Sh...
on Thursday July 23, 2026 @06:57PM (#49029198)
that's why in clinical trials you first do phase 1 human subjects where they are healthy and take small sub-therapeutic doses to test safety/tolerability. once it's established safe in humans they do phase 2 where they test if it works on sick people. Yeah I know this is different with transduction but they could at least test the vector first, maybe they did? Maybe some kind of lentivirus vector
Re:Couple pay >$800k for a gene-editing therapy for their daughter. Sh...
on Thursday July 23, 2026 @06:54PM (#49029166)
kinda sounds like in vivo test driven dev